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Article title
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Abstract
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Keywords
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Introduction
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Animal models of Loss-of-function diseases
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Duchenne muscular dystrophy
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Spinal muscular atrophy
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Inherited retinal diseases
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Animal models of dominant diseases
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Myotonic dystrophy type 1
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Parkinson’s disease
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Huntington’s disease
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Amyotrophic lateral sclerosis (ALS)
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Charcot-Marie-Tooth disease
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Conclusion
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Conflict of interests
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References
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Author contributions